Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. BOSTON — A medicine increasingly used to ...

Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have persisted for more than two years for some patients.

Doctors have linked a boy's tumor to a gene therapy, but say the rare risks need to be weighed against the profound benefits ...

A gene therapy based on GLP-1 (glucagon-like peptide-1), which could treat diabetes and obesity with a single lifetime dose, ...

The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time treatment that proved to be life-changing for a small number of children in a ...

The FDA has approved Otarmeni, the first-ever gene therapy for genetic hearing loss caused by the OTOF gene, for both pediatric and adult patients after positive results.

Dr. Marty Makary noted it had "record speed approval," the fastest approval of any gene therapy device combination in U.S.

A breakthrough FDA-approved treatment is changing how genetic deafness is treated.

The New York Times is reporting that a single infusion could suppress HIV for years. This gene therapy uses the same ...

New POLARIS Phase I/II data presented at ASGCT show ETX101 gene therapy reducing seizures and improving neurodevelopment in ...